Andelyn Biosciences, a cell and gene therapy contract development and manufacturing organization (CDMO), has been selected by UMass Chan Medical School to use its suspension AAV Curator Platform to manufacture clinical grade AAV9-CSA vector to treat Cockayne syndrome. The nonprofit patient-advocacy organization, Riaan Research Initiative, has provided the largest known donation ever made toward the development of a treatment for Cockayne syndrome. The gift from Riaan Research Initiative and ...